- CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
Science advances (2017-04-26)
Yu Zhang, Chengzu Long, Hui Li, John R McAnally, Kedryn K Baskin, John M Shelton, Rhonda Bassel-Duby, Eric N Olson
PMID28439558
ABSTRACT
Duchenne muscular dystrophy (DMD), caused by mutations in the X-linked dystrophin gene (